亚甲基四氢叶酸还原酶和胸苷酸合成酶基因多态预测氟尿嘧啶为基础化疗方案治疗晚期胃癌疗效关系的研究(英文)

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目的观察亚甲基四氢叶酸还原酶(MTHFR)(C677T、A1298C)和胸苷酸合成酶(TS 3’-UTR)多态与5-FU为基础化疗方案及晚期胃癌敏感性的关系。方法选取173例晚期胃癌患者,所有病例均接受5-FU为基础化疗方案(FOLFOX,FP和DCF方案)化疗。在化疗前获取外周血白细胞DNA。采用PCR-RELP检测基因型。在2个基因中共检测了9种遗传多态。173例中检测了MTHFR(C677T、A1298C)和TS(3’-TUR)多态。结果所有患者化疗总有效率为35.8%。DCF方案的有效率显著高于FP和FOLFOX方案(55.8%vs 27.1%,31.1%;P=0.006)。MTHFR C677T T/T基因型患者的有效率显著高于C/C和C/T基因型(73.3%vs 28.0%;P=0.000)。在MTHFR A1298C中,A/A基因型患者的有效率显著高于C/C和A/C基因型(41.8%vs 21.6%,P=0.011),在TS 3’-UTR中,-6/-6bp和-6/+6bp基因型患者的有效率显著高于+6/+6 bp基因型(40.3%vs 17.6%,P=0.014)。FOLFOX和FP方案中,MTHFR C677T T/T基因型患者的有效率均显著高于C/C和C/T基因型(P=0.008;P=0.000),但在DCF方案中没有发现差异。在MTHFR C/T和C/C基因型中,DCF方案的有效率显著高于FP和FOLFOX方案(P=0.000)。MTHFR C677T T/T基因型患者的Ⅲ-Ⅳ度呕吐(66.7%)和口腔炎(30.0%)发生率显著高于C/C和C/T基因型(41.3%,9.8%;P=0.011,0.003)。MTHFR A1298C A/A基因型患者的Ⅲ-Ⅳ度口腔炎(17.2%)和腹泻(13.9%)发生率同样显著高于A/C和C/C基因(3.9%,2.0%;P=0.025,0.026)。TS 3’-UTR的不同多态之间没有发现毒性差异。结论检测外周血白细胞DNA中的MTHFR和TS基因多态能预测以5-FU为基础化疗方案治疗晚期胃癌的有效性和化疗相关的毒性反应。 Objective To investigate the relationship between polymorphisms of methylenetetrahydrofolate reductase (MTHFR) (C677T, A1298C) and thymidylate synthase (TS 3’-UTR) and 5-FU-based chemotherapy regimen and the sensitivity of advanced gastric cancer. Methods A total of 173 patients with advanced gastric cancer were enrolled in this study. All patients underwent chemotherapy with 5-FU-based chemotherapy (FOLFOX, FP and DCF regimens). Peripheral blood leukocyte DNA is obtained before chemotherapy. Genotypes were detected by PCR-RELP. Nine genetic polymorphisms were detected in two genes. Of 173 cases, MTHFR (C677T, A1298C) and TS (3’-TUR) polymorphisms were examined. Results The total effective rate of chemotherapy in all patients was 35.8%. The efficiency of the DCF regimen was significantly higher than that of the FP and FOLFOX regimens (55.8% vs 27.1%, 31.1%; P = 0.006). Patients with MTHFR C677T T / T genotype were significantly more effective than C / C and C / T genotypes (73.3% vs 28.0%; P = 0.000). In MTHFR A1298C, the efficiency of A / A genotype patients was significantly higher than that of C / C and A / C genotypes (41.8% vs 21.6%, P = 0.011) Patients with 6bp and -6 / + 6bp genotypes were significantly more effective than the + 6 / + 6 bp genotype (40.3% vs 17.6%, P = 0.014). In the FOLFOX and FP regimens, the efficiency of the MTHFR C677T T / T genotype was significantly higher for the C / C and C / T genotypes (P = 0.008; P = 0.000), but no differences were found in the DCF regimen. In the MTHFR C / T and C / C genotypes, the efficiency of the DCF regimen was significantly higher than that of the FP and FOLFOX regimens (P = 0.000). The incidence of grade Ⅲ-Ⅳ vomiting (66.7%) and stomatitis (30.0%) in MTHFR C677T T / T genotype was significantly higher than that in C / C and C / T genotypes (41.3%, 9.8% 0.003). The incidence of grade Ⅲ-Ⅳ stomatitis (17.2%) and diarrhea (13.9%) in patients with MTHFR A1298C A / A genotype was also significantly higher than those in A / C and C / C genes (3.9%, 2.0% 0.026). Toxic differences were not found between the different polymorphisms of the TS 3’-UTR. Conclusion Detection of polymorphisms of MTHFR and TS in peripheral leukocyte DNA can predict the efficacy of 5-FU-based chemotherapy in the treatment of advanced gastric cancer and chemotherapy-related toxicities.
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